Gene therapy for Pyruvate Kinase Deficiency and Congenital Dyserythropoietic Anemia Type II
Speakers: José Carlos Segovia, Mercedes Dessy Rodríguez, Oscar Quintana Bustamante, Isabel Ojeda-Pérez
Target:
Health professionals
Subnetworks: Red blood cell defects
Disease Groups: Congenital dyserythropoietic anemia, Rare constitutional hemolytic anemia due to pyruvate kinase deficiency